- Grants since 2016
- 611
- Awarded, last 5 years (where amounts are published)
- €94.6M
- Funded works, last 5 years
- 5 837
- Funded works, all time
- 8 569
Grants
2016–2019 · grant
TTR-FAP Italian Registry: a collaborative network for definition of natural history, psychosocial burden, standards of care and clinical trials
Giuseppe Vita · University of Messina
2016–2021 · grant
Expanding genetically engineered HSC: from translation to biology and back
Bernhard Gentner · Fondazione Centro San Raffaele
2016–2021 · grant
Tigem Behavioural Core
Elvira De Leonibus · Telethon Institute Of Genetics And Medicine (tigem)
2016–2021 · grant
Pharmacological modulation of ion transport to treat the basic defect in cystic fibrosis
Luis Juan Vicente Galietta · Telethon Institute Of Genetics And Medicine (tigem)
2016–2017 · grant
Generation of a novel mouse model for SAM syndrome
Caterina Missero · University of Campania "Luigi Vanvitelli"
2016–2021 · grant
Integrative genomic approaches to human cell fate reprogramming in development and genetic diseases
Davide Cacchiarelli · Telethon Institute Of Genetics And Medicine (tigem)
2016–2021 · grant
Role of lysosomal processes in skeletal development and diseases, and identification of therapeutic approaches for the treatment of skeletal manifestation in Lysosomal Storage Disorders
Carmine Settembre · Telethon Institute Of Genetics And Medicine (tigem)
2016–2021 · grant
Restoration of hematopoiesis following gene correction in beta-thal
Giuliana Ferrari · Fondazione Centro San Raffaele
2016–2021 · grant
Regulation of hematopoiesis in normal and stressed conditions
Giuliana Ferrari · Fondazione Centro San Raffaele
2016–2021 · grant
Mechanisms of dynamic regulation of TFEB and mTORC1 activity
Diego Di Bernardo · Telethon Institute Of Genetics And Medicine (tigem)
2016–2017 · grant
Investigating the contribution of the telomeric gene AKTIP in progeroid syndromes with unknown mutations
Isabella Saggio · Sapienza University of Rome
2016–2021 · grant
Novel strategies to generate tolerogenic DC for Ag-specific immunotherapy
Silvia Gregori · Fondazione Centro San Raffaele
2016–2019 · grant
Clinical efficacy of NIV and modafinil on excessive daytime sleepiness: a multicenter, randomized, double-blind, placebo-controlled clinical trial in DM1
Valeria Sansone · Centro Clinico Nemo
2016–2021 · grant
In vivo induction of Ag-specific tolerance by hepatocyte-targeted gene transfer
Silvia Gregori · Fondazione Centro San Raffaele
2016–2021 · grant
Use of MSC to optimize transplantation outcome of gene edited-HSC
Maria Ester Bernardo · Fondazione Centro San Raffaele
2016–2021 · grant
Mechanisms of enhanced HSC transduction and nucleic acid sensing
Anna Christina Kajaste-Rudnitski · Fondazione Centro San Raffaele
2016–2021 · grant
Tigem High Content Screening Facility
Diego Medina · Telethon Institute Of Genetics And Medicine (tigem)
2016–2021 · grant
HSPC biology: in vivo clonal tracking and lineage modeling
Alessandro Aiuti · Fondazione Centro San Raffaele
2016–2019 · grant
Modulating Neuregulin-1 Signals to Treat Hereditary Demyelinating Neuropathies
Carla Taveggia · Fondazione Centro San Raffaele
2016–2021 · grant
Congenital liver disease
Nicola Brunetti-Pierri · Telethon Institute Of Genetics And Medicine (tigem)
2016–2021 · grant
Mechanistic principles of permanent epigenetic silencing and their exploitation to improve targeted epigenetic editing
Angelo Lombardo · Fondazione Centro San Raffaele
2016–2021 · grant
Clinical network and Registry for Trial Readiness in Spinal and Bulbar Muscle Atrophy
Caterina Mariotti · Fondazione Istituto Neurologico Carlo Besta - Irccs
2016–2021 · grant
Tigem Advanced Microscopy and Imaging
Roman Polishchuk · Telethon Institute Of Genetics And Medicine (tigem)
2016–2019 · grant
Rescue of Fanconi Bickel Syndrome by targeting glucose transport in the renal proximal tubule
Francesco Trepiccione · University of Campania "Luigi Vanvitelli"
2016–2017 · grant
Generation of an in vitro model to investigate replicative stress as the possible molecular mechanism underlying Schimke immunoosseous dysplasia
Pietro Pichierri · Istituto Superiore di Sanità
2016–2021 · grant
Disease' mechanisms and pharmacological targeting of behavioral symptoms in Sanfilippo Syndrome
Ivan Conte · Telethon Institute Of Genetics And Medicine (tigem)
2016–2021 · grant
Tigem Next Generation Sequencing Facility
Vincenzo Nigro · Telethon Institute Of Genetics And Medicine (tigem)
2015–2021 · grant
Defining the role of the cellular prion protein at the intersection of several neurodegenerative diseases
Emiliano Biasini · University of Trento
2015–2021 · grant
Functional and structural studies of human CLC chloride proteins involved in genetic diseases
Alessandra Picollo · National Research Council
2015–2020 · grant
Gene therapy and long term evaluation of different dietary regimens in a Glycogen Storage Disease Type III KO mouse model
Giacomo Comi · Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico
2015–2020 · grant
Oxidative stress and Cerebral Cavernous Malformations (CCM): from disease mechanisms toward prevention and treatment
Saverio Francesco Retta · Ospedale San Luigi Gonzaga
2015–2022 · grant
Parkinson's disease at the synaptic site: short and long term impact of pathological LRRK2 kinase activity
Giovanni Piccoli · University of Trento
2015–2020 · grant
Crosstalks between DNA damage response and retroelements activity in the pathogenesis of Aicardi-Goutières Syndrome
Marco Muzi Falconi · University of Milan
2015–2020 · grant
Familial hemiplegic migraine mechanisms
Daniela Pietrobon · University of Padua
2014–2025 · grant
IMPROVED GENETIC MANIPULATION OF HSC FOR EX VIVO GENE THERAPY
Bernhard Gentner · San Raffaele Telethon Institute For Gene Therapy - Sr-tiget
2014–2020 · grant
MECHANISMS OF FIBROSIS IN MUSCULAR DYSTROPHIES
Stefano Biressi · University of Trento
2014–2025 · grant
GLP - GOOD LABORATORY PRACTICE
Patrizia Cristofori · San Raffaele Telethon Institute For Gene Therapy - Sr-tiget
2013–2021 · grant
Targeting Akt signaling in muscle to identify new therapeutic strategies for spinal and bulbar muscular atrophy
Maria Pennuto · University of Trento
2013–2020 · grant
DISSECTING THE MOLECULAR FUNCTION OF MUTANT HUNTINGTIN WITH STEM CELLS
Graziano Martello · University of Padua
2012–2025 · grant
INTRACEREBRAL ADMINISTRATION OF LENTIVIRAL VECTORS IN AN ANIMAL MODEL: A BIODISTRIBUTION STUDY
Angela Gritti · San Raffaele Telethon Institute For Gene Therapy - Sr-tiget